Events & Presentations Presentations Corporate Presentation - March 2024 Spacer Past events April 2, 2024 at 9:50 AM EDT Cantor Virtual Muscular Dystrophy Symposium Listen to Webcast March 20, 2024 at 8:30 AM EDT Stifel 2024 Virtual CNS Days Listen to Webcast February 14, 2024 at 2:40 PM EST Oppenheimer 34th Annual Healthcare Life Sciences Conference Listen to Webcast February 8, 2024 at 11:00 AM EST Guggenheim Healthcare Talks | 6th Annual Biotechnology Conference Listen to Webcast January 9, 2024 at 2:15 PM PST 42nd Annual J.P. Morgan Healthcare Conference Listen to Webcast J.P. Morgan Healthcare Presentation 3.4 MB January 3, 2024 at 8:00 AM EST ACHIEVE and DELIVER Clinical Data Update Listen to Webcast ACHIEVE and DELIVER Clinical Data Update Presentation 7.9 MB November 28, 2023 at 1:30 PM EST Piper Sandler 35th Annual Healthcare Conference Listen to Webcast November 14, 2023 at 4:45 PM EST Stifel 2023 Healthcare Conference Listen to Webcast October 12, 2023 at 9:30 AM EDT Jefferies Inaugural Biotech CNS/Neuro Summit Listen to Webcast October 3, 2023 at 11:00 AM EDT Chardan 7th Annual Genetic Medicines Listen to Webcast September 11, 2023 at 4:15 PM EDT Morgan Stanley 21st Annual Global Healthcare Conference Listen to Webcast June 8, 2023 at 2:00 PM EDT Jefferies Healthcare Conference Listen to Webcast May 24, 2023 at 9:00 AM EDT 2023 Annual Meeting of Stockholders May 10, 2023 at 2:35 PM EDT BofA Securities 2023 Healthcare Conference Listen to Webcast April 4, 2023 at 10:10 AM EDT Guggenheim Genomic Medicines and Rare Disease Days Listen to Webcast March 29, 2023 at 11:30 AM EDT Stifel 2023 CNS Days Listen to Webcast March 13, 2023 at 2:40 PM EDT Oppenheimer 33rd Annual Healthcare Conference Listen to Webcast January 10, 2023 at 3:00 PM PST 41st Annual J.P. Morgan Healthcare Conference Listen to Webcast J.P. Morgan Healthcare Conference Presentation 4.5 MB November 29, 2022 at 11:00 AM EST Piper Sandler 34th Annual Healthcare Conference Listen to Webcast November 16, 2022 at 11:30 AM EST Stifel 2022 Healthcare Conference Listen to Webcast November 16, 2022 at 7:20 AM EST Jefferies London Healthcare Conference Listen to Webcast November 9, 2022 at 2:00 PM EST Credit Suisse 31st Annual Healthcare Conference Listen to Webcast